UnravelingRare

A podcast produced by Unravel Biosciences to highlight patients, families, and other stakeholders critical to addressing orphan disorders.

Episode 01:

Rett Syndrome in Latin America

Episode 02:

Boys with Rett Syndrome

Episode 03:

AP-4 Hereditary Spastic Paraplegia: solving multiple disorders at once

Episode 04:

CHOPS Syndrome and Synergies in Drug Development

COMING SOON!

Episode 05:

In vivo drug screening is a critical path to clinical efficacy

COMING SOON!

Episode 06:

Using N-of-1 clinical trial design as a derisking strategy